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PTC Therapeutics International LimitedEU/1/22/1653/001

Main Information

Trade NameUpstaza
Active SubstancesEladocagene Exuparvovec
Dosage FormSolution for infusion
Licence HolderPTC Therapeutics International Limited
Licence NumberEU/1/22/1653/001

Group Information

ATC Code


License statusAuthorised
Licence Issued18/07/2022
Legal statusProduct subject to prescription which may not be renewed (A)
Supply StatusSupply through pharmacies only
Advertising StatusAdvertising to healthcare professionals only
Conditions of LicenceMedicinal product subject to restricted medical prescription (see Annex I: Summary of Product Characteristics, section 4.2).
Marketing StatusUnknown


Summary of Product CharacteristicsSearch EMA website
Package LeafletSearch EMA website
Public Assessment ReportSearch EMA website
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